Mice play an important role in the development of therapies for rare diseases like Phelan-McDermid Syndrome. These little guys make a big difference in getting us closer to a cure!

What is Phelan-McDermid Syndrome? What are its symptoms? How many people are affected? These are questions that caregivers of individuals with Phelan-McDermid Syndrome hear all of the time.

We’re excited to announce the launch of CureSHANK’s two signature programs to address the major gap areas in drug development for Phelan-McDermid Syndrome:

We are proud to be participating in Healx's webinar on the development of in vitro models for rare disease research on August 13, 2020.