Geraldine Bliss Geraldine Bliss

Pioneering Progress: Insights from ASGCT 2025 on the Future of PMS Therapeutics

Last week, Geraldine Bliss attended the American Society of Gene and Cell Therapy (ASGCT) Annual Meeting in New Orleans on behalf of CureSHANK. Her participation reflects our unwavering commitment to staying at the forefront of research and innovation for the Phelan-McDermid syndrome (PMS) community. ASGCT is the premier international forum for advancements in gene and cell therapy, and Geraldine’s presence ensured that the unique needs of our community were represented in critical conversations. Her key takeaways—from gene editing to emerging delivery strategies—offer an invaluable window into the promising (and complex) path ahead for PMS therapeutics.

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Newsletters CureSHANK Newsletters CureSHANK

Newsletter: Fall 2023

Registration is now open for our Fall 2023 Community webinar on Thursday, October 5 at 8pmEST/5pmCST. Please join us to learn about what we have accomplished so far in 2023 (including updates from our recent Epilepsy meeting); what we are planning for the future; and how you can get involved!

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Learn More Abby Lievense Learn More Abby Lievense

What's a Knockout Mouse?

Mice play an important role in the development of therapies for rare diseases like Phelan-McDermid Syndrome. These little guys make a big difference in getting us closer to a cure!

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